Publications

Schlichtenbrede FC, da Cruz L, Stephens C, Smith AJ, Georgiadis A, Thrasher AJ, Bain-bridge JW, Seeliger MW, Ali RR. Long term evaluation of retinal function in Prph2 Rd2/Rd2 mice following AAV-mediated gene replacement therapy. J Gene Med 2003; 5: 757-764.

Bemelmans AP, Kostic C, Crippa SV, Hauswirth WW, Lem J, Seeliger MW, Wenzel A, Arsenijevic Y. Lentiviral-mediated transfer of the RPE65 cDNA rescues both survival and function of cone photoreceptors in a mouse model of Leber congenital amaurosis. PLoS Med 2006;3: 1892-1903.

Janssen A, Min SH, Molday LL, Tanimoto N, Seeliger MW, Hauswirth WW, Molday RS, Weber BH. Effect of late-stage therapy on disease progression in AAV-mediated rescue of photoreceptor cells in the retinoschisin-deficient mouse. Mol Ther 2008; 16:1010-1017.

Michalakis S*, Mühlfriedel R*, Tanimoto N, Krishnamoorthy V, Koch S, Fischer MD, Becirovic E, Bai L, Huber G, Beck SC, Fahl E, Büning H, Paquet-Durand F, Zong X, Gollisch T, Biel M, Seeliger MW (2010). Restoration of cone vision in the CNGA3-/- mouse model of congenital complete lack of cone photoreceptor function. Mol Ther. 18:2057-63.

Koch S, Sothilingam V, Garcia Garrido M, Tanimoto N, Becirovic E, Koch F, Seide C, Beck SC, Seeliger MW, Biel M, Mühlfriedel R*, Michalakis S* (2012). Gene therapy restores vision and delays degeneration in the CNGB1-/- mouse model of retinitis pigmentosa. Hum Mol Genet 21: 4486-4496.